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Disease Reportsinborn urea cycle disorders
MeSH D056806 - inborn urea cycle disorders
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Competitive Landscape
Events Timeline
Commercial
Clinical Trials
Competitive landscape
D000592:Inborn errors amino acid metabolism
$
Success rate
D020739:Metabolic brain diseases inborn
0 Companies
0 Drugs
Success rate
D056806: 
Inborn urea cycle disorders
$
Success rate
D020159:Citrullinemia
$
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D020162:Hyperargininemia
0 Companies
0 Drugs
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D020163:Ornithine carbamoyltransferase deficiency disease
$
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D020165:Carbamoyl-phosphate synthase i deficiency disease
$
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D056807:Argininosuccinic aciduria
0 Companies
0 Drugs
Success rate
Events Timeline
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Commercial
Company Name
Drug Name
Trade Name
Patent Expires
Approval Date
Revenue
Period
Immedica PharmaGlycerol phenylbutyrate Ravicti  2015-11-26   
Clinical Trials
Historical Success Rate
Phase 1
100%
2/2
Phase 2
75%
3/4
Phase 3
50%
2/4
Approved: 1Overall Success rate: 38%
All Clinical Trials
No data
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